Daniel Cressy says today is a life-changing day. The man in his 20s received a gene therapy transfusion Wednesday at Manning Family Children's Hospital that doctors say should cure his sickle cell ...
ATLANTA -- Patients with transfusion-dependent β-thalassemia (TDT) who received a gene therapy achieved normal or near-normal levels of total hemoglobin and transfusion independence, with stable iron ...
Please provide your email address to receive an email when new articles are posted on . Thompson described beta-thalassemia as a severe chronic inherited blood disorder due to one of many mutations in ...
Memories of classical ballet performances dance in Wanda Sihanath's head when she thinks about her childhood in Elgin, Illinois. She remembers balancing at the barre to Beethoven and pirouetting to ...
At the time of the interim analysis, 91.4% (32/35) of patients achieved transfusion independence for 12 consecutive months. The Food and Drug Administration (FDA) has approved Casgevy ™ (exagamglogene ...
The development and approval of gene therapies has been a potential game changer for patients with beta-thalassaemia who have been dependent on regular red blood cell transfusions -- a substantial ...
All four parent studies are complete, and all patients have transitioned to a long-term follow-up study (LTF-303) SOMERVILLE, Mass.--(BUSINESS WIRE)--Updated data from bluebird bio inc.’s (NASDAQ: ...
UK: The SWiFT trial has found that prehospital transfusion of whole blood did not improve survival or reduce massive transfusion rates compared to component therapy in major traumatic hemorrhage.
Blood transfusion therapy remains an indispensable intervention in the management of sickle cell disease (SCD), mitigating life‐threatening complications such as vaso‐occlusive crises and stroke. The ...
Over 90 percent of patients with transfusion-dependent thalassemia, an inherited blood disorder, no longer needed monthly blood transfusions years after receiving gene therapy, according to an ...
A novel gene therapy promoted transfusion independence in more than 90 percent of adult and pediatric patients with transfusion-dependent beta-thalassemia, according to a recent clinical trial ...
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