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It is specifically designed to help children with spinal muscular atrophy. The suit even has built-in sensors allowing it to mimic human movement. Produced by Claudia Romeo More from UK Spanish ...
Despite significant advancements in spinal muscular atrophy (SMA) management, unmet needs persist, especially for patients ...
"We are working with urgency to deliver the potentially transformative benefits of apitegromab to children and adults with (spinal muscular atrophy) in the US, Europe and around the world." ...
Purpose: X-linked infantile spinal-muscular atrophy (XL-SMA) is a rare disorder, which presents with the clinical characteristics of hypotonia, areflexia, and multiple congenital contractures ...
The mutation that causes Spinal Muscular Atrophy (SMA) can be detected in ... with many decisions regarding the health of affected children and the well-being of other family members.
a Novartis gene therapy for the fatal neuron-wasting disease spinal muscular atrophy. It heralded a new era of genetic medicine, allowing some children who may have once died in infancy to grow up.