Despite significant advancements in spinal muscular atrophy (SMA) management, unmet needs persist, especially for patients ...

Affordable generic version of SMA drug Risdiplam soon available in India, offering hope to patients and activists.

FDA-approved treatments for spinal muscular atrophy differ in their mechanisms of action, safety profiles, and administration ...

All money supports the researchers’ quest to find a treatment and cure. Spinal Muscular Atrophy (SMA) is a deadly, genetic disease that causes a dramatic loss of strength and, in most cases ...

Supreme Court examines pleas challenging 50 lakh cap on Centre's assistance for treating rare diseases like SMA.

Imagine the joy of holding your newborn for the first time, only to hear doctors say your baby would live to the age of two.

Funding medical research is about more than just numbers. It's real people,” says Ryan Manriquez, president of the UC ...

It's that time of year when you can become a Hero for Hope and donate to ABC15's annual Telethon for Phoenix Children's ...

The FDA has accepted for Priority Review the BLA for apitegromab for the improvement of motor function in patients with spinal muscular atrophy.

Intrathecal treatment with a vector-based gene therapy was associated with a greater improvement in motor function at 52 weeks compared with sham in patients aged 2 to 18 years with spinal muscular ...

The Supreme Court will review the Rs 50 lakh cap on the central government's aid for treating rare diseases like SMA. The ...

The bench said pharma firm M/s F Hoffmann-La Roche Ltd, which manufactures the SMA drug Risdiplam priced at Rs 6.2 lakh a ...